Doctors have used the up-and-coming gene therapy tool CRISPR in a human for the first time as part of an ongoing clinical trial to treat a genetic condition called Leber congenital amaurosis (LCA). LCA is an inherited eye disorder that affects the retina (the layer of tissue at the back of the eye that detects…

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September is Newborn Screening Awareness Month! Get educated by learning of a few of the disorders included in newborn screening and how they can be treated. In the United States, when a baby is born he/she is screened for an array of conditions that, if known about, could dramatically improve or save the baby’s life.…

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